New HD drug could be ‘ground-breaking’

A potentially ground-breaking trial that is being hailed as the most important development in HD since the HD gene was identified back in 1993 has been announced by pharma companies Ionis and Roche. It involves the first human trial of a huntingtin-lowering drug, IONIS-HTTRx, which demonstrated a reduction in mutant huntingtin in the nervous system. […]